To Cure LGMD2B
We are researching individualized gene-editing stem cell therapy for LGMD2B.
What is LGMD2B?
LGMD2B is incurable muscular dystrophy caused by some mutations in the DYSF gene.
Why is LGMD2B first?
Because the founder of this company is a patient of LGMD2B and so are his siblings. So the founder has a strong passion to succeed in this research as a patient himself, as a brother of patients, and as a father who is concerned if his children would inherit his gene mutation. Not only that, he will donate his AdMSCs and be a volunteer patient for the research.
How to cure LGMD2B.
There have been so many kinds of approaches to find any kind of treatment to cure LGMD2B or mitigate the symptom, yet there is no significant solution for the rare disease LGMD2B.
But, fortunately, ever since so many new biotechnologies about Stem Cells and Gene-Editing have been found and improved as well as the IND regulation by FDA has become to allow ‘Individualized Medicine’ for various rare diseases, we recently could come up with an advanced approach to cure LGMD2B.
More than LGMD2B.
We will build the process and platform based on the research results to cure other rare muscular disorders caused by gene mutations as well.